Duchenne Muscular Dystrophy

Reimbursement: You will be compensated for your time and commitment plus reasonable travel expenses or transport provided.

About This clinical research study

Clinical trials are research projects, performed as a way of bringing about progress in medicine and research. Clinical research projects make it possible to scientifically assess the properties of a study medication, to demonstrate the effectiveness and safety of a treatment or a medical device, or to learn more about a disease and methods to diagnose and monitor it.

Here at MAC we are looking for people who would like to take part in our future clinical trials researching potential new treatments for Duchenne muscular dystrophy.

Duchenne muscular dystrophy (DMD), also known as Duchenne’s, DMD disease, or Duchenne disease, is one of the most common muscular dystrophy types. It is a genetic (inherited) condition, mainly affecting males with Duchenne muscular dystrophy life expectancy being in their 30’s, the charity Duchenne UK estimates there are 2,500 people living with the condition in Britain.

Duchenne muscular dystrophy causes the body to make a much shorter, inactive version of a protein known as dystrophin, which is essential for protecting the working muscles and results in progressive muscle weakness, other Duchenne muscular dystrophy symptoms often include scoliosis (curving of the spine), dilated cardiomyopathy and respiratory problems. Physiotherapy, exercise, and medications, such as corticosteroids, are the most usual Duchenne muscular dystrophy treatments, but there is currently no cure for the condition.

There is an urgent need for additional treatments to help those living with the condition. Current research on Duchenne muscular dystrophy treatments often focuses around DMD clinical trial gene therapy or exon skipping therapy.

More information will be available on the clinical trial once approval of the research is granted by the regulatory bodies in the UK.

Reimbursement: You will be compensated for your time and commitment plus reasonable travel expenses or transport provided.


Greater Manchester

Therapy Area

Duchenne Muscular Dystrophy

Gender and Age

Males aged 16+

A full description of the clinical trial will be given before you decide to take part, during an appointment at a MAC clinic. This will include you receiving the patient information sheet and an opportunity to ask the clinical research doctor any questions.

If you have Duchenne’s, you may be eligible to participate in one of our future clinical trials.

There is no obligation to take part in a clinical trial and you are free to withdraw at any time.

By taking part in a clinical trial, you may be helping in the development of pioneering new treatments that may help improve the quality of life for people with DMD.

Reimbursement: You will be compensated for your time and commitment plus reasonable travel expenses or transport provided.

Key Inclusion Criteria

Key Exclusion Criteria

Other eligibility criteria will apply. Please contact MAC for more information.

If you are eligible you will receive a comprehensive health screen. Your GP will be fully informed of your participation and provided with any information relevant to your healthcare.

Please note: Currently we have no clinical trials in Duchenne’s available, we will contact you with regards to your application to establish eligibility for any future studies.

If you would like more information, please fill in the form below and we will be in touch…

Alternatively, please call our recruitment team on freephone 0800 633 5507.

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